Gene therapy with adeno-associated virus (aav) vectors has demonstrated safety and long-term efficacy in a number of tri-als across target organs, including eye, liver, skeletal muscle, and the Search across a wide variety of disciplines and sources: Articles, theses, books, abstracts and court opinions.

Edmonson, s. Thurlings, p. Eduard ayuso, federico mingozzi, fatima bosch centre for animal biotechnology and gene therapy (cbateg) laboratori d'enginyeria genΓ¨tica animal i terΓ pia gΓ¨nica department of biochemistry Ò€¦